| Targeted gene therapy and cell reprogramming in Fanconi anemia P Rio, R Baños, A Lombardo, O Quintana‐Bustamante, L Alvarez, ... EMBO molecular medicine 6 (6), 835-848, 2014 | 91 | 2014 |
| NHEJ-mediated repair of CRISPR-Cas9-induced DNA breaks efficiently corrects mutations in HSPCs from patients with fanconi anemia FJ Román-Rodríguez, L Ugalde, L Alvarez, B Díez, MJ Ramírez, ... Cell Stem Cell 25 (5), 607-621. e7, 2019 | 74 | 2019 |
| Therapeutic gene editing in CD34+ hematopoietic progenitors from Fanconi anemia patients B Diez, P Genovese, FJ Roman‐Rodriguez, L Alvarez, G Schiroli, ... EMBO molecular medicine 9 (11), 1574-1588, 2017 | 58 | 2017 |
| Transfer of gene-corrected T cells corrects humoral and cytotoxic defects in patients with X-linked lymphoproliferative disease N Panchal, B Houghton, B Diez, S Ghosh, I Ricciardelli, AJ Thrasher, ... Journal of Allergy and Clinical Immunology 142 (1), 235-245. e6, 2018 | 44 | 2018 |
| A novel high-content analysis tool reveals Rab8-driven cytoskeletal reorganization through Rho GTPases, calpain and MT1-MMP JJ Bravo-Cordero, M Cordani, SF Soriano, B Díez, C Muñoz-Agudo, ... Journal of cell science 129 (8), 1734-1749, 2016 | 35 | 2016 |
| Therapeutic gene editing in CD34 (+) hematopoietic progenitors from Fanconi anemia patients. EMBO Mol Med 9: 1574–1588 B Diez, P Genovese, FJ Roman-Rodriguez, L Alvarez, G Schiroli, ... | 19 | 2017 |
| BCR–JAK2 drives a myeloproliferative neoplasm in transplanted mice Á Cuesta‐Domínguez, D León‐Rico, L Álvarez, B Díez, I Bodega‐Mayor, ... The Journal of pathology 236 (2), 219-228, 2015 | 8 | 2015 |
| Preclinical safety and efficacy of lentiviral-mediated gene therapy for leukocyte adhesion deficiency type I C Mesa-Núñez, C Damián, M Fernández-García, B Díez, G Rao, ... Molecular Therapy-Methods & Clinical Development 26, 459-470, 2022 | 3 | 2022 |
| Efficacy of a gene therapy approach using a humanized model of Fanconi anemia R Banos, A Valeri, L Alvarez, B Diez, RM Pujol, R Sanchez-Dominguez, ... Human Gene Therapy 23 (10), A111-A111, 2012 | 1 | 2012 |
| Homology Independent Gene Editing Strategies to Correct Hematopoietic Stem Cells from Fanconi Anemia A Patients L Ugalde, E Karasu, S Siegner, A Clemens, L Alvarez, B Diez, JA Bueren, ... HUMAN GENE THERAPY 32 (19-20), A25-A25, 2021 | | 2021 |
| Broad applicability of NHEJ-mediated gene editing to correct mutations in a variety of Fanconi Anemia genes L Ugalde, FJ Roman-Rodriguez, L Alvarez, B Diez, MJ Ramirez, ... HUMAN GENE THERAPY 30 (11), A13-A13, 2019 | | 2019 |
| Optimized manufacturing of lentiviral corrected hematopoietic stem cells under GMP conditions B Diez, M Fernandez-Garcia, R Yanez, S Navarro, P Rio, JA Bueren HUMAN GENE THERAPY 30 (11), A84-A84, 2019 | | 2019 |
| NHEJ-mediated gene editing phenotypically corrects Fanconi anemia A patients' haematopoietic stem and progenitor cells FJ Roman-Rodriguez, L Ugalde, L Alvarez, B Diez, M Bogliolo, ... HUMAN GENE THERAPY 29 (12), A103-A104, 2018 | | 2018 |
| NHEJ-Mediated Gene Editing: An Efficient Approach to Correct Mutations in Hematopoietic Stem and Progenitor Cells from Patients with Fanconi Anemia FJ Roman-Rodriguez, L Ugalde, L Alvarez, B Diez, C Risueño, M Corton, ... Available at SSRN 3285807, 2018 | | 2018 |
| Improvements in the Transduction Conditions of Human Hematopoietic Progenitors with the CPcoRPKW-17 Therapeutic Lentiviral Vector to be Used in a Pyruvate Kinase Deficiency … S Navarro, O Quintana-Bustamante, M Villanueva, B Diez, ... MOLECULAR THERAPY 26 (5), 100-100, 2018 | | 2018 |
| British Society for Gene and Cell Therapy Annual Conference and Joint UK Regenerative Medicine Platform Meeting Royal Welsh College of Music & Drama Cardiff, Wales, United … W Qasim, A Nathwani, M Cavazzana, R Buckle, S Harding, A Baker, ... Human Gene Therapy 28 (8), A1-A36, 2017 | | 2017 |
| Development of T cell mediated gene therapy for correction of humoral and cytotoxic defects in X-linked lymphoproliferative disease (XLP) N Panchal, B Houghton, B Diez, A Thrasher, B Gaspar, C Booth Annual Conference of the British-Society-for-Gene-and-Cell-Therapy/Joint UK …, 2017 | | 2017 |
| T Cell Gene Therapy Corrects Humoral and Cytotoxic Defects in X-Linked Lymphoproliferative Disease (XLP) N Panchal, B Hougton, B Diez, AJ Thrasher, HB Gaspar, C Booth 20th Annual Meeting of the American-Society-of-Gene-and-Cell-Therapy (ASGCT), 2017 | | 2017 |
| A Novel Gene Therapy Approach of Fanconi Anemia Hematopoietic Stem Cells Based on NHEJ-Mediated Gene Editing FJ Roman-Rodriguez, B Diez, L Alvarez, R Torres-Ruiz, M Corton, ... MOLECULAR THERAPY 25 (5), 79-79, 2017 | | 2017 |
| NHEJ-mediated gene editing as a new alternative for the hematopoietic gene therapy in Fanconi anemia FJ Roman-Rodriguez, B Diez, L Alvarez, R Torres-Ruiz, M Corton, ... HUMAN GENE THERAPY 27 (11), A130-A130, 2016 | | 2016 |
