| Correction of the sickle cell disease mutation in human hematopoietic stem/progenitor cells MD Hoban, GJ Cost, MC Mendel, Z Romero, ML Kaufman, AV Joglekar, ... Blood 125 (17), 2597-2604, 2015 | 369 | 2015 |
| Correction of the sickle cell disease mutation in human hematopoietic stem/progenitor cells MD Hoban, GJ Cost, MC Mendel, Z Romero, ML Kaufman, AV Joglekar, ... Blood 125 (17), 2597-2604, 2015 | 369 | 2015 |
| Gene therapy for adenosine deaminase–deficient severe combined immune deficiency: clinical comparison of retroviral vectors and treatment plans F Candotti, KL Shaw, L Muul, D Carbonaro, R Sokolic, C Choi, ... Blood 120 (18), 3635-3646, 2012 | 279 | 2012 |
| CRISPR/Cas9-Mediated Correction of the Sickle Mutation in Human CD34+ cells MD Hoban, D Lumaquin, CY Kuo, Z Romero, J Long, M Ho, CS Young, ... Molecular Therapy, 2016 | 225 | 2016 |
| Modeling initiation of Ewing sarcoma in human neural crest cells C von Levetzow, X Jiang, Y Gwye, G von Levetzow, L Hung, A Cooper, ... PLoS One 6 (4), e19305, 2011 | 199 | 2011 |
| Prostate cancer originating in basal cells progresses to adenocarcinoma propagated by luminal-like cells T Stoyanova, AR Cooper, JM Drake, X Liu, AJ Armstrong, KJ Pienta, ... Proceedings of the National Academy of Sciences 110 (50), 20111-20116, 2013 | 186 | 2013 |
| BMI-1 promotes ewing sarcoma tumorigenicity independent of CDKN2A repression D Douglas, JHR Hsu, L Hung, A Cooper, D Abdueva, J van Doorninck, ... Cancer research 68 (16), 6507-6515, 2008 | 157 | 2008 |
| Site-specific gene editing of human hematopoietic stem cells for X-linked hyper-IgM syndrome CY Kuo, JD Long, B Campo-Fernandez, S de Oliveira, AR Cooper, ... Cell reports 23 (9), 2606-2616, 2018 | 136 | 2018 |
| β-globin gene transfer to human bone marrow for sickle cell disease Z Romero, F Urbinati, S Geiger, AR Cooper, J Wherley, ML Kaufman, ... The Journal of clinical investigation 123 (8), 3317-3330, 2013 | 113 | 2013 |
| Preclinical demonstration of lentiviral vector-mediated correction of immunological and metabolic abnormalities in models of adenosine deaminase deficiency DA Carbonaro, L Zhang, X Jin, C Montiel-Equihua, S Geiger, M Carmo, ... Molecular Therapy 22 (3), 607-622, 2014 | 97 | 2014 |
| Preclinical Demonstration of Lentiviral Vector-mediated Correction of Immunological and Metabolic Abnormalities in Models of Adenosine Deaminase Deficiency HB Gaspar, L Zhang, AJ Thrasher, X Wang, S Senadheera, ... Nature Publishing Group, 2014 | 97* | 2014 |
| Clinical efficacy of gene-modified stem cells in adenosine deaminase–deficient immunodeficiency KL Shaw, E Garabedian, S Mishra, P Barman, A Davila, D Carbonaro, ... The Journal of clinical investigation 127 (5), 1689-1699, 2017 | 93 | 2017 |
| Highly efficient large-scale lentiviral vector concentration by tandem tangential flow filtration AR Cooper, S Patel, S Senadheera, K Plath, DB Kohn, RP Hollis Journal of virological methods 177 (1), 1-9, 2011 | 90 | 2011 |
| Intercohort gene expression co-analysis reveals chemokine receptors as prognostic indicators in Ewing's sarcoma IM Bennani-Baiti, A Cooper, ER Lawlor, M Kauer, J Ban, DNT Aryee, ... Clinical Cancer Research 16 (14), 3769-3778, 2010 | 73 | 2010 |
| Stem Cell Research & Therapy JP Awe, PC Lee, C Ramathal, A Vega-Crespo, J Durruthy-Durruthy, ... | 68* | 2013 |
| Generation and characterization of transgene-free human induced pluripotent stem cells and conversion to putative clinical-grade status JP Awe, PC Lee, C Ramathal, A Vega-Crespo, J Durruthy-Durruthy, ... Stem cell research & therapy 4 (4), 1, 2013 | 68 | 2013 |
| Reactivating Fetal Hemoglobin Expression in Human Adult Erythroblasts Through BCL11A Knockdown Using Targeted Endonucleases CF Bjurström, M Mojadidi, J Phillips, C Kuo, S Lai, GR Lill, A Cooper, ... Molecular Therapy—Nucleic Acids 5 (8), e351, 2016 | 61 | 2016 |
| From skin biopsy to neurons through a pluripotent intermediate under good manufacturing practice protocols S Karumbayaram, P Lee, SF Azghadi, AR Cooper, M Patterson, DB Kohn, ... Stem cells translational medicine 1 (1), 36-43, 2012 | 59 | 2012 |
| Swab-Seq: A high-throughput platform for massively scaled up SARS-CoV-2 testing Joshua S. Bloom1, 2, 3, Laila Sathe4, Chetan Munugala1, 2, Eric M. Jones3, Molly Gasperini3 … L Guo, J Boocock, M Hochman, SW Simpkins, I Lin, N LaPierre, D Hong, ... | 54* | |
| Long-term in vivo monitoring of mouse and human hematopoietic stem cell engraftment with a human positron emission tomography reporter gene MN McCracken, EH Gschweng, E Nair-Gill, J McLaughlin, AR Cooper, ... Proceedings of the National Academy of Sciences 110 (5), 1857-1862, 2013 | 51 | 2013 |
Donald KohnUCLA chla nihVerified email at mednet.ucla.edu
