| Design of efficacious somatic cell genome editing strategies for recessive and polygenic diseases J Carlson-Stevermer, A Das, AA Abdeen, D Fiflis, BI Grindel, S Saxena, ... Nature communications 11 (1), 6277, 2020 | 10 | 2020 |
| Nonviral base editing of KCNJ13 mutation preserves vision in a model of inherited retinal channelopathy M Kabra, PK Shahi, Y Wang, D Sinha, A Spillane, GA Newby, S Saxena, ... The Journal of Clinical Investigation 133 (19), 2023 | 3 | 2023 |
| Profiling Cell Type Specificity and Adverse Events of Genome Editing Nucleases in the Brain and Retina Using Single Cell Transcriptomics K Saha, K Gimse, J Shin, Y Wang, JM Metzger, K Mueller, E Capowski, ... ENVIRONMENTAL AND MOLECULAR MUTAGENESIS 63, 63-63, 2022 | | 2022 |
| CRISPR base editing as a potential therapeutic approach for Kir7. 1 channelopathy M Kabra, PK Shahi, A SPILLANE, Y Wang, D Sinha, GA Newby, S Saxena, ... Investigative Ophthalmology & Visual Science 62 (8), 1483-1483, 2021 | | 2021 |
| Design of Efficacious Somatic Cell Genome Editing Strategies for Recessive and Polygenic Diseases A Das, J Carlson-Stevermer, A Abdeen, D Fiflis, B Grindel, S Saxena, ... MOLECULAR THERAPY 29 (4), 204-205, 2021 | | 2021 |
| Nanoparticle mediated in vitro and in vivo CRISPR base correction of LCA16 causing nonsense mutation rescues Kir7. 1 channel function M Kabra, PK Shahi, Y Wang, D Sinha, A Spillane, GA Newby, S Saxena, ... | | |
| Email: pattnaik@ wisc. edu M Kabra, PK Shahi, Y Wang, D Sinha, A Spillane, GA Newby, S Saxena, ... | | |
