| Delivery of siRNA to the mouse brain by systemic injection of targeted exosomes L Alvarez-Erviti, Y Seow, HF Yin, C Betts, S Lakhal, MJA Wood Nature biotechnology 29 (4), 341-345, 2011 | 4538 | 2011 |
| Delivery of therapeutic oligonucleotides with cell penetrating peptides P Boisguérin, S Deshayes, MJ Gait, L O'Donovan, C Godfrey, CA Betts, ... Advanced drug delivery reviews 87, 52-67, 2015 | 271 | 2015 |
| Pip6-PMO, a new generation of peptide-oligonucleotide conjugates with improved cardiac exon skipping activity for DMD treatment C Betts, AF Saleh, AA Arzumanov, SM Hammond, C Godfrey, ... Molecular Therapy-Nucleic Acids 1, 2012 | 233 | 2012 |
| Pip5 transduction peptides direct high efficiency oligonucleotide-mediated dystrophin exon skipping in heart and phenotypic correction in mdx mice HF Yin, AF Saleh, C Betts, P Camelliti, Y Seow, S Ashraf, A Arzumanov, ... Molecular therapy 19 (7), 1295-1303, 2011 | 167 | 2011 |
| A fusion peptide directs enhanced systemic dystrophin exon skipping and functional restoration in dystrophin-deficient mdx mice HF Yin, HM Moulton, C Betts, Y Seow, J Boutilier, PL Iverson, MJA Wood Human molecular genetics 18 (22), 4405-4414, 2009 | 157 | 2009 |
| Expression analysis in multiple muscle groups and serum reveals complexity in the microRNA transcriptome of the mdx mouse with implications for therapy TC Roberts, KEM Blomberg, G McClorey, SEL Andaloussi, C Godfrey, ... Molecular Therapy-Nucleic Acids 1, 2012 | 151 | 2012 |
| How much dystrophin is enough: the physiological consequences of different levels of dystrophin in the mdx mouse C Godfrey, S Muses, G McClorey, KE Wells, T Coursindel, RL Terry, ... Human molecular genetics 24 (15), 4225-4237, 2015 | 141 | 2015 |
| Current understanding of molecular pathology and treatment of cardiomyopathy in duchenne muscular dystrophy TLE Van Westering, CA Betts, MJA Wood Molecules 20 (5), 8823-8855, 2015 | 115 | 2015 |
| Functional rescue of dystrophin-deficient mdx mice by a chimeric peptide-PMO HF Yin, HM Moulton, C Betts, T Merritt, Y Seow, S Ashraf, QS Wang, ... Molecular Therapy 18 (10), 1822-1829, 2010 | 86 | 2010 |
| Diaphragm rescue alone prevents heart dysfunction in dystrophic mice A Crisp, HF Yin, A Goyenvalle, C Betts, HM Moulton, Y Seow, A Babbs, ... Human molecular genetics 20 (3), 413-421, 2011 | 78 | 2011 |
| Optimization of peptide nucleic acid antisense oligonucleotides for local and systemic dystrophin splice correction in the mdx mouse HF Yin, C Betts, AF Saleh, GD Ivanova, H Lee, Y Seow, D Kim, MJ Gait, ... Molecular Therapy 18 (4), 819-827, 2010 | 78 | 2010 |
| Cell-penetrating peptide conjugates of steric blocking oligonucleotides as therapeutics for neuromuscular diseases from a historical perspective to current prospects of treatment MJ Gait, AA Arzumanov, G McClorey, C Godfrey, C Betts, S Hammond, ... nucleic acid therapeutics 29 (1), 1-12, 2019 | 74 | 2019 |
| Identification of novel, therapy-responsive protein biomarkers in a mouse model of Duchenne muscular dystrophy by aptamer-based serum proteomics AML Coenen-Stass, G McClorey, R Manzano, CA Betts, A Blain, AF Saleh, ... Scientific reports 5 (1), 17014, 2015 | 67 | 2015 |
| Prevention of exercised induced cardiomyopathy following Pip-PMO treatment in dystrophic mdx mice CA Betts, AF Saleh, CA Carr, SM Hammond, AML Coenen-Stass, ... Scientific reports 5 (1), 8986, 2015 | 61 | 2015 |
| Selective release of muscle-specific, extracellular microRNAs during myogenic differentiation AML Coenen-Stass, CA Betts, YF Lee, I Mäger, MP Turunen, ... Human Molecular Genetics 25 (18), 3960-3974, 2016 | 58 | 2016 |
| Detection and quantification of extracellular microRNAs in murine biofluids TC Roberts, AML Coenen-Stass, CA Betts, MJA Wood Biological procedures online 16, 1-15, 2014 | 54 | 2014 |
| Interventions targeting glucocorticoid-Krüppel-like factor 15-branched-chain amino acid signaling improve disease phenotypes in spinal muscular atrophy mice LM Walter, MO Deguise, KE Meijboom, CA Betts, N Ahlskog, ... EBioMedicine 31, 226-242, 2018 | 47 | 2018 |
| Uniform sarcolemmal dystrophin expression is required to prevent extracellular microRNA release and improve dystrophic pathology TLE van Westering, Y Lomonosova, AML Coenen‐Stass, CA Betts, ... Journal of Cachexia, Sarcopenia and Muscle 11 (2), 578-593, 2020 | 25 | 2020 |
| Context dependent effects of chimeric peptide morpholino conjugates contribute to dystrophin exon-skipping efficiency HF Yin, P Boisguerin, HM Moulton, C Betts, Y Seow, J Boutilier, Q Wang, ... Molecular Therapy-Nucleic Acids 2, 2013 | 22 | 2013 |
| Peptide-conjugated phosphodiamidate oligomer-mediated exon skipping has benefits for cardiac function in mdx and Cmah-/-mdx mouse models of Duchenne … AM Blain, E Greally, G McClorey, R Manzano, CA Betts, C Godfrey, ... PLoS One 13 (6), e0198897, 2018 | 21 | 2018 |
