In situ gene therapy via AAV-CRISPR-Cas9-mediated targeted gene regulation AM Moreno, X Fu, J Zhu, D Katrekar, YRV Shih, J Marlett, J Cabotaje, ... Molecular Therapy 26 (7), 1818-1827, 2018 | 147 | 2018 |
Immune-orthogonal orthologues of AAV capsids and of Cas9 circumvent the immune response to the administration of gene therapy AM Moreno, N Palmer, F Alemán, G Chen, A Pla, N Jiang, W Leong Chew, ... Nature biomedical engineering 3 (10), 806-816, 2019 | 94 | 2019 |
Long-lasting analgesia via targeted in situ repression of NaV1.7 in mice AM Moreno, F Alemán, GF Catroli, M Hunt, M Hu, A Dailamy, A Pla, ... Science translational medicine 13 (584), eaay9056, 2021 | 75 | 2021 |
Insulin-regulated serine and lipid metabolism drive peripheral neuropathy MK Handzlik, JM Gengatharan, KE Frizzi, GH McGregor, C Martino, ... Nature 614 (7946), 118-124, 2023 | 52 | 2023 |
Oligonucleotide conjugated multi-functional adeno-associated viruses D Katrekar, AM Moreno, G Chen, A Worlikar, P Mali Scientific reports 8 (1), 3589, 2018 | 47 | 2018 |
Therapeutic genome engineering via CRISPR‐Cas systems AM Moreno, P Mali Wiley Interdisciplinary Reviews: Systems Biology and Medicine 9 (4), e1380, 2017 | 42 | 2017 |
Exploring protein orthogonality in immune space: a case study with AAV and Cas9 orthologs AM Moreno, N Palmer, F Alemán, G Chen, A Pla, WL Chew, M Law, ... BioRxiv, 245985, 2018 | 14 | 2018 |
Programmatic introduction of parenchymal cell types into blood vessel organoids A Dailamy, U Parekh, D Katrekar, A Kumar, D McDonald, A Moreno, ... Stem Cell Reports 16 (10), 2432-2441, 2021 | 11 | 2021 |
Gene therapies to reduce chronic pain: are we there yet? A Vega-Loza, C Van, A M Moreno, F Aleman Pain Management 10 (4), 209-212, 2020 | 5 | 2020 |
Author Correction: Immune-orthogonal orthologues of AAV capsids and of Cas9 circumvent the immune response to the administration of gene therapy AM Moreno, N Palmer, F Alemán, G Chen, A Pla, N Jiang, WL Chew, ... Nature Biomedical Engineering 3 (10), 842-842, 2019 | 5 | 2019 |
Hepatic serine and lipid metabolism drive diabetic peripheral neuropathy C Metallo, M Handzlik, J Gengatharan, K Frizzi, G McGregor, C Martino, ... | | 2022 |
Long-lasting Analgesia via Targeted in vivo Epigenetic Repression of Nav1. 7 AM Morenoa, GF Catrolib, F Alemána, A Plaa, SA Wollerb, M Hua, ... | | |