Human pluripotent stem cell-derived acinar/ductal organoids generate human pancreas upon orthotopic transplantation and allow disease modelling M Hohwieler, A Illing, PC Hermann, T Mayer, M Stockmann, L Perkhofer, ... Gut 66 (3), 473-486, 2017 | 220 | 2017 |
Uridine depletion and chemical modification increase Cas9 mRNA activity and reduce immunogenicity without HPLC purification S Vaidyanathan, KT Azizian, AKMA Haque, JM Henderson, A Hendel, ... Molecular Therapy-Nucleic Acids 12, 530-542, 2018 | 218 | 2018 |
Chemically modified hCFTR mRNAs recuperate lung function in a mouse model of cystic fibrosis AKMA Haque, A Dewerth, JS Antony, J Riethmüller, GR Schweizer, ... Scientific reports 8 (1), 16776, 2018 | 70 | 2018 |
Gene correction of HBB mutations in CD34+ hematopoietic stem cells using Cas9 mRNA and ssODN donors JS Antony, N Latifi, AKMA Haque, A Lamsfus-Calle, A Daniel-Moreno, ... Molecular and cellular pediatrics 5, 1-7, 2018 | 65 | 2018 |
Comparative targeting analysis of KLF1, BCL11A, and HBG1/2 in CD34+ HSPCs by CRISPR/Cas9 for the induction of fetal hemoglobin A Lamsfus-Calle, A Daniel-Moreno, JS Antony, T Epting, L Heumos, ... Scientific reports 10 (1), 10133, 2020 | 52 | 2020 |
CRISPR/Cas9-modified hematopoietic stem cells—present and future perspectives for stem cell transplantation A Daniel-Moreno, A Lamsfus-Calle, J Raju, JS Antony, R Handgretinger, ... Bone Marrow Transplantation 54 (12), 1940-1950, 2019 | 37 | 2019 |
Mannose-binding lectin and susceptibility to schistosomiasis JS Antony, O Ojurongbe, H van Tong, EA Ouf, T Engleitner, AA Akindele, ... The Journal of infectious diseases 207 (11), 1675-1683, 2013 | 36 | 2013 |
IL-4 haplotype-590T,-34T and intron-3 VNTR R2 is associated with reduced malaria risk among ancestral indian tribal populations AN Jha, VK Singh, N Kumari, A Singh, J Antony, H van Tong, S Singh, ... PloS one 7 (10), e48136, 2012 | 34 | 2012 |
Transcriptomic profile of cystic fibrosis patients identifies type I interferon response and ribosomal stalk proteins as potential modifiers of disease severity. AJS Kormann MSD, Dewerth A, Eichner F, Baskaran P, Hector A, Regamey N ... PLOS ONE 12 (8), e0183526, 2017 | 33 | 2017 |
Hematopoietic stem cell gene therapy: The optimal use of lentivirus and gene editing approaches A Lamsfus-Calle, A Daniel-Moreno, G Urena-Bailen, J Raju, JS Antony, ... Blood reviews 40, 100641, 2020 | 27 | 2020 |
Modified mRNA as a new therapeutic option for pediatric respiratory diseases and hemoglobinopathies JS Antony, A Dewerth, A Haque, R Handgretinger, MSD Kormann Molecular and Cellular Pediatrics 2, 1-6, 2015 | 26 | 2015 |
Molecular Evidence of Wolbachia Endosymbiosis in Mansonella perstans in Gabon, Central Africa C Gehringer, A Kreidenweiss, A Flamen, JS Antony, MP Grobusch, ... The Journal of infectious diseases 210 (10), 1633-1638, 2014 | 26 | 2014 |
CRISPR/Cas9 technology: towards a new generation of improved CAR-T cells for anticancer therapies G Ureña-Bailén, A Lamsfus-Calle, A Daniel-Moreno, J Raju, P Schlegel, ... Briefings in functional genomics 19 (3), 191-200, 2020 | 24 | 2020 |
Association of Ficolin-2 Serum Levels and FCN2 Genetic Variants with Indian Visceral Leishmaniasis A Mishra, JS Antony, P Sundaravadivel, HV Tong, CG Meyer, RD Jalli, ... PLoS One 10 (5), e0125940, 2015 | 23 | 2015 |
CRISPR/Cas9 system: A promising technology for the treatment of inherited and neoplastic hematological diseases JS Antony, AKMA Haque, A Lamsfus‐Calle, A Daniel‐Moreno, M Mezger, ... Advances in Cell and Gene Therapy 1 (1), e10, 2018 | 19 | 2018 |
Lectin complement protein Collectin 11 (CL-K1) and susceptibility to urinary schistosomiasis JS Antony, O Ojurongbe, PG Kremsner, TP Velavan PLoS Neglected Tropical Diseases 9 (3), e0003647, 2015 | 18 | 2015 |
Somatic Reversion of a Novel IL2RG Mutation Resulting in Atypical X-Linked Combined Immunodeficiency Y Hou, HP Gratz, G Ureña-Bailén, PG Gratz, K Schilbach-Stückle, ... Genes 13 (1), 35, 2021 | 15 | 2021 |
Preclinical evaluation of CRISPR-edited CAR-NK-92 cells for off-the-shelf treatment of AML and B-ALL G Ureña-Bailén, JM Dobrowolski, Y Hou, A Dirlam, A Roig-Merino, ... International Journal of Molecular Sciences 23 (21), 12828, 2022 | 13 | 2022 |
Mannose-binding Lectin (MBL) as a susceptible host factor influencing Indian Visceral Leishmaniasis A Mishra, JS Antony, P Gai, P Sundaravadivel, AN Jha, L Singh, ... Parasitology international 64 (6), 591-596, 2015 | 13 | 2015 |
A mutation-agnostic hematopoietic stem cell gene therapy for metachromatic leukodystrophy JS Antony, A Daniel-Moreno, A Lamsfus-Calle, J Raju, M Kaftancioglu, ... The CRISPR Journal 5 (1), 66-79, 2022 | 12 | 2022 |